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Meijboom, KE, Volpato, V, Monzón-Sandoval, J, Hoolachan, JM, Hammond, SM, Abendroth, F, de Jong, OG, Hazell, G, Ahlskog, N, Wood, MJA, Webber, C and Bowerman, M ORCID: https://orcid.org/0000-0002-3579-6403 (2021) Combining multi-omics and drug perturbation profiles to identify muscle-specific treatments for spinal muscular atrophy. JCI Insight, 6 (13). pp. 1-24.

Winkelsas, AM, Grunseich, C, Harmison, GG, Chwalenia, K, Rinaldi, C, Hammond, SM, Johnson, K, Bowerman, M ORCID: https://orcid.org/0000-0002-3579-6403, Arya, S, Talbot, K, Wood, MJ and Fischbeck, KH (2021) Targeting the 5’ untranslated region of SMN2 as a therapeutic strategy for spinal muscular atrophy. Molecular Therapy: Nucleic Acids, 23. pp. 731-742.

Bowerman, M, Walter, LM, Deguise, M-O, Meijboom, KE, Betts, CA, Ahlskog, N, van Westering, TLE, Hazell, G, McFall, E, Kordala, A, Hammond, SM, Abendroth, F, Murray, LM, Shorrock, HK, Prosdocimo, DA, Haldar, SM, Jain, MK, Gillingwater, TH, Claus, P, Kothary, R and Wood, MJA (2018) Interventions Targeting Glucocorticoid-Krüppel-like Factor 15-Branched-Chain Amino Acid Signaling Improve Disease Phenotypes in Spinal Muscular Atrophy Mice. EBioMedicine, 31. pp. 226-242.

Hammond, SM, Hazell, G, Shabanpoor, F, Saleh, AF, Bowerman, M, Sleigh, JN, Meijboom, KE, Zhou, H, Muntoni, F, Talbot, K, Gait, MJ and Wood, MJA (2016) Systemic peptide-mediated oligonucleotide therapy improves long-term survival in spinal muscular atrophy. PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA, 113 (39). 10962 - 10967.