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Nafchi, NAM, Chilcott, EM, Owen, SJ ORCID: https://orcid.org/0000-0001-9671-7054, Fuller, HR ORCID: https://orcid.org/0000-0001-8868-896X, Bowerman, M ORCID: https://orcid.org/0000-0002-3579-6403 and Yáñez-Muñoz, RJ (2023) Enhanced expression of the human Survival motor neuron 1 gene from a sequence-optimised cDNA transgene in vitro and in vivo. Gene Therapy (Basingstoke). (In Press)

Bowerman, M, Becker, CG, Yáñez-Muñoz, RJ, Ning, K, Wood, MJA, Gillingwater, TH, Talbot, K and UK SMA Research Consortium, . (2017) Therapeutic strategies for spinal muscular atrophy: SMN and beyond. Disease Models and Mechanisms, 10 (8). 943 - 954.